Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000700468 | SCV000829225 | pathogenic | Danon disease | 2018-05-09 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (ExAC no frequency). This sequence change creates a premature translational stop signal (p.Trp46*) in the LAMP2 gene. It is expected to result in an absent or disrupted protein product. This variant has been observed in an individual affected with Danon disease (PMID: 23504560). A different variant (c.138G>A) giving rise to the same protein effect observed here (p.Trp46*) has been reported in an individual affected with Danon disease (PMID: 15889279). Loss-of-function variants in LAMP2 are known to be pathogenic (PMID: 21415759). For these reasons, this variant has been classified as Pathogenic. |