Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000786769 | SCV002236776 | pathogenic | Danon disease | 2022-02-09 | criteria provided, single submitter | clinical testing | ClinVar contains an entry for this variant (Variation ID: 635277). This premature translational stop signal has been observed in individual(s) with Danon disease (PMID: 23955649). This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Val64Asnfs*11) in the LAMP2 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in LAMP2 are known to be pathogenic (PMID: 21415759). For these reasons, this variant has been classified as Pathogenic. |
Cytoplasmic Inheritance Laboratory, |
RCV000786769 | SCV000924630 | likely pathogenic | Danon disease | 2019-06-02 | no assertion criteria provided | clinical testing | The variant is absent in publicly available population databases (gnomAD, 1000Genomes). It was found in a woman with dilatation cardiomyopathy. NM_002294.2:c.190_191delAC creates a premature stop codon at position 11 of the new reading frame - p.V64NfsX11. It means the truncated protein lacks the transmembrane domain, cytosolic tail and most part of the luminal domain. Such rearrangement will lead to loss of function of LAMP2. |