Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Biochemistry and Genetic Laboratory, |
RCV001310276 | SCV001499897 | likely pathogenic | MPI-congenital disorder of glycosylation | 2020-11-19 | no assertion criteria provided | clinical testing | The Gly57Arg variant in the MPI gene was reported in a French patient in a compound heterozygosity state with a known splicing variant c.345 + 1G> A. The c.169G>A, p.Gly57Arg variant was absent from the gnomAD and dbSNP databases. In addition, PMI activity was found to be collapsed and intermediate for both parents. These results are in favor of a MPI-CDG of autosomal recessive transmission. The disease was diagnosed following a deep vein thrombosis of the right lower limb at the age of 12 years associated with low antithrombin III level and a subsequent hepatic exploration showed slight increased hepatic elasticity and transaminase ALAT. |