Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Center for Statistical Genetics, |
RCV001449850 | SCV001652887 | likely pathogenic | Gaucher disease due to saposin C deficiency | 2021-04-14 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV002541741 | SCV003473164 | pathogenic | Sphingolipid activator protein 1 deficiency | 2024-01-15 | criteria provided, single submitter | clinical testing | This sequence change replaces glutamic acid, which is acidic and polar, with alanine, which is neutral and non-polar, at codon 359 of the PSAP protein (p.Glu359Ala). This variant is present in population databases (rs765744298, gnomAD 0.04%). This missense change has been observed in individual(s) with atypical Gaucher disease (PMID: 35456468). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 991967). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on PSAP protein function. For these reasons, this variant has been classified as Pathogenic. |
Natera, |
RCV001280271 | SCV001467436 | uncertain significance | Metachromatic leukodystrophy | 2020-04-11 | no assertion criteria provided | clinical testing |