Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000429762 | SCV000535969 | uncertain significance | not provided | 2021-01-05 | criteria provided, single submitter | clinical testing | Has not been previously published as pathogenic or benign to our knowledge; Not observed at a significant frequency in large population cohorts (Lek et al., 2016); In silico analysis, which includes protein predictors and evolutionary conservation, supports that this variant does not alter protein structure/function |
Hudson |
RCV000850403 | SCV000992600 | uncertain significance | Spondyloepiphyseal dysplasia, Stanescu type | 2018-04-17 | criteria provided, single submitter | research | |
Ambry Genetics | RCV002525501 | SCV003556351 | uncertain significance | Inborn genetic diseases | 2021-06-25 | criteria provided, single submitter | clinical testing | The c.991A>C (p.T331P) alteration is located in exon 9 (coding exon 8) of the ALDH18A1 gene. This alteration results from a A to C substitution at nucleotide position 991, causing the threonine (T) at amino acid position 331 to be replaced by a proline (P). Based on insufficient or conflicting evidence, the clinical significance of this alteration remains unclear. |
Baylor Genetics | RCV003147460 | SCV003835808 | likely pathogenic | Autosomal recessive complex spastic paraplegia type 9B | 2022-10-23 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003766464 | SCV004571923 | likely pathogenic | Cutis laxa, autosomal dominant 3; Autosomal dominant spastic paraplegia type 9; de Barsy syndrome | 2023-08-27 | criteria provided, single submitter | clinical testing | ClinVar contains an entry for this variant (Variation ID: 392663). This missense change has been observed in individuals with clinical features of autosomal recessive hereditary spastic paraplegia (PMID: 36067040). It has also been observed to segregate with disease in related individuals. This variant is present in population databases (rs765380273, gnomAD 0.003%). This sequence change replaces threonine, which is neutral and polar, with proline, which is neutral and non-polar, at codon 331 of the ALDH18A1 protein (p.Thr331Pro). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on ALDH18A1 protein function. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. Experimental studies are conflicting or provide insufficient evidence to determine the effect of this variant on ALDH18A1 function (PMID: 36067040). |
OMIM | RCV003152603 | SCV003841149 | pathogenic | ALDH18A1-related de Barsy syndrome | 2023-03-14 | no assertion criteria provided | literature only |