Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Lupski Lab, |
RCV000203265 | SCV000256752 | pathogenic | Pontocerebellar hypoplasia type 1A | 2013-10-14 | criteria provided, single submitter | research | Segregates with the phenotype in affected family |
Gene |
RCV003441782 | SCV000617743 | pathogenic | not provided | 2024-03-27 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect, as the V236M variant results in loss of kinase activity (PMID: 31527692); Reported in trans with another VRK1 variant in two siblings with microcephaly and severe, rapidly progressive distal symmetric polyneuropathy with normal intellect in published literature (PMID: 24126608); Not observed at significant frequency in large population cohorts (gnomAD); Missense variants in this gene are a common cause of disease and they are underrepresented in the general population; This variant is associated with the following publications: (PMID: 24970098, 27281532, 25609612, 26583493, 34169149, 30617279, 30847374, 31178479, 27149842, 35641352, 31560180, 31090908, 24126608, 31527692) |
Labcorp Genetics |
RCV000203265 | SCV000836197 | pathogenic | Pontocerebellar hypoplasia type 1A | 2024-01-26 | criteria provided, single submitter | clinical testing | This sequence change replaces valine, which is neutral and non-polar, with methionine, which is neutral and non-polar, at codon 236 of the VRK1 protein (p.Val236Met). This variant is present in population databases (rs771364038, gnomAD 0.01%). This missense change has been observed in individual(s) with clinical features of distal hereditary motor neuropathy (PMID: 24126608; Invitae). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 218924). An algorithm developed to predict the effect of missense changes on protein structure and function (PolyPhen-2) suggests that this variant is likely to be disruptive. Experimental studies have shown that this missense change affects VRK1 function (PMID: 31527692). For these reasons, this variant has been classified as Pathogenic. |
Centogene AG - |
RCV000203265 | SCV002059512 | likely pathogenic | Pontocerebellar hypoplasia type 1A | 2020-07-14 | criteria provided, single submitter | clinical testing | |
Ambry Genetics | RCV002517363 | SCV003566935 | uncertain significance | Inborn genetic diseases | 2021-12-16 | criteria provided, single submitter | clinical testing | The c.706G>A (p.V236M) alteration is located in exon 8 (coding exon 7) of the VRK1 gene. This alteration results from a G to A substitution at nucleotide position 706, causing the valine (V) at amino acid position 236 to be replaced by a methionine (M). Based on insufficient or conflicting evidence, the clinical significance of this alteration remains unclear. |
Natera, |
RCV000203265 | SCV002093696 | uncertain significance | Pontocerebellar hypoplasia type 1A | 2021-02-15 | no assertion criteria provided | clinical testing | |
OMIM | RCV003387514 | SCV004098884 | pathogenic | Neuronopathy, distal hereditary motor, autosomal recessive 10 | 2013-12-01 | no assertion criteria provided | literature only |