Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Rady Children's Institute for Genomic Medicine, |
RCV000853345 | SCV000996207 | pathogenic | Kabuki syndrome 1 | 2018-10-16 | criteria provided, single submitter | clinical testing | This frameshifting variant in exon 12 of 54 introduces a premature stop codon and is therefore predicted to result in loss of normal protein function. This variant has not been previously reported or functionally characterized in the literature to our knowledge, but loss of function variants are an established mechanism of disease for KMT2D. The variant is absent from the ExAC and gnomAD population databases and thus is presumed to be rare. Analysis of the parental samples was negative for the variant, indicating this variant likely occurred as a de novo event. Based on the available evidence, the c.3968dupG, p.Arg1324Ter variant is classified as Pathogenic. |