Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000147314 | SCV000194687 | likely pathogenic | Iron accumulation in brain | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Mendelics | RCV000537119 | SCV002518871 | pathogenic | Infantile neuroaxonal dystrophy | 2022-05-04 | criteria provided, single submitter | clinical testing | |
Broad Center for Mendelian Genomics, |
RCV002515979 | SCV003761471 | uncertain significance | PLA2G6-associated neurodegeneration | 2023-01-24 | criteria provided, single submitter | curation | The p.Arg710Cys variant in PLA2G6 has been reported in 2 individuals with PLA2G6-associated neurodegeneration (PMID: 31493945), and has been identified in 0.003% (1/30616) of South Asian chromosomes by the Genome Aggregation Database (gnomAD, http://gnomad.broadinstitute.org; dbSNP ID: rs587784347). Although this variant has been seen in the general population in a heterozygous state, its frequency is low enough to be consistent with a recessive carrier frequency. This variant has also been reported in ClinVar (Variation ID#: 159759) and has been interpreted as pathogenic by Genetic Services Laboratory (University of Chicago) and Undiagnosed Diseases Network (NIH). Of the 2 affected individuals, one of those was a homozygote, which increases the likelihood that the p.Arg710Cys variant is pathogenic (PMID: 31493945; ClinVar ID#: 159759). Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. In summary, the clinical significance of the p.Arg710Cys variant is uncertain. ACMG/AMP Criteria applied: PM3_supporting, PP3, PM2_supporting (Richards 2015). |
Undiagnosed Diseases Network, |
RCV000537119 | SCV000622145 | likely pathogenic | Infantile neuroaxonal dystrophy | 2016-04-13 | no assertion criteria provided | clinical testing | Variant previously reported in two other patients with this phenotype tested the by the same laboratory (one listed in ClinVar). One patient was reportedly homozygous for this variant, while the other was compound heterozygous. Variant is rare (2 heterozygotes in ExAC). Likely pathogenicity given patient’s phenotype consistent with known phenotype associated with gene, infantile neuroaxonal dystrophy (MIM 256600), homozygous rare variant in patient with consanguineous parents, variant reportedly identified in two other patients with this phenotype. |