Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000147317 | SCV000194690 | pathogenic | Iron accumulation in brain | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003507259 | SCV004300017 | pathogenic | Infantile neuroaxonal dystrophy | 2023-12-02 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with tryptophan, which is neutral and slightly polar, at codon 745 of the PLA2G6 protein (p.Arg745Trp). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individual(s) with clinical features of infantile neuroaxonal dystrophy (PMID: 16783378, 24800972, 29859652). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 159762). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt PLA2G6 protein function with a positive predictive value of 80%. For these reasons, this variant has been classified as Pathogenic. |
Molecular Genetics Lab, |
RCV003883135 | SCV004697615 | likely pathogenic | Infantile neuroaxonal dystrophy; Neurodegeneration with brain iron accumulation 2B; Autosomal recessive Parkinson disease 14 | criteria provided, single submitter | clinical testing | ||
Biochemical Molecular Genetic Laboratory, |
RCV000985141 | SCV001133130 | likely pathogenic | Neurodegeneration with brain iron accumulation 2B | 2019-09-26 | no assertion criteria provided | clinical testing |