Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001383893 | SCV001583215 | pathogenic | Hermansky-Pudlak syndrome 2 | 2023-02-18 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Ala541Serfs*25) in the AP3B1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in AP3B1 are known to be pathogenic (PMID: 16507770, 23403622). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with Hermansky-Pudlak syndrome (PMID: 14566336). ClinVar contains an entry for this variant (Variation ID: 1071422). For these reasons, this variant has been classified as Pathogenic. |
OMIM | RCV001383893 | SCV000026937 | pathogenic | Hermansky-Pudlak syndrome 2 | 2003-11-01 | no assertion criteria provided | literature only |