Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000798436 | SCV000938053 | uncertain significance | Frontotemporal dementia and/or amyotrophic lateral sclerosis 1; Paget disease of bone 2, early-onset | 2023-09-04 | criteria provided, single submitter | clinical testing | This missense change has been observed in individual(s) with clinical features of SQSTM1-related conditions (PMID: 33601107). In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is not expected to disrupt SQSTM1 protein function. ClinVar contains an entry for this variant (Variation ID: 644501). This variant is present in population databases (rs199663339, gnomAD 0.01%). This sequence change replaces threonine, which is neutral and polar, with methionine, which is neutral and non-polar, at codon 221 of the SQSTM1 protein (p.Thr221Met). |
Gene |
RCV001772056 | SCV002003693 | uncertain significance | not provided | 2021-04-07 | criteria provided, single submitter | clinical testing | In silico analysis supports that this missense variant does not alter protein structure/function; Previously reported as a variant of uncertain significance in an individual with Parkinsonism (Picillo et al., 2021); This variant is associated with the following publications: (PMID: 33601107, 25796131) |
Prevention |
RCV004735808 | SCV005346354 | uncertain significance | SQSTM1-related disorder | 2024-04-11 | no assertion criteria provided | clinical testing | The SQSTM1 c.662C>T variant is predicted to result in the amino acid substitution p.Thr221Met. This variant was reported in an individual with parkinsonism and cognitive-behavioral syndrome (Picillo et al. 2021. PubMed ID: 33601107). This variant is reported in 0.012% of alleles in individuals of African descent in gnomAD. At this time, the clinical significance of this variant is uncertain due to the absence of conclusive functional and genetic evidence. |