Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV003151706 | SCV003840674 | pathogenic | not provided | 2023-03-10 | criteria provided, single submitter | clinical testing | Frameshift variant in the C-terminus predicted to cause a protein extension as the last 74 amino acids are replaced with 105 incorrect amino acids; Not observed in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 15888479, 19191321, 15121777, 18157832, 12640453) |
Prevention |
RCV003415666 | SCV004117842 | pathogenic | PHOX2B-related disorder | 2023-03-14 | criteria provided, single submitter | clinical testing | The PHOX2B c.722_759del38 variant is predicted to result in a frameshift and premature protein termination (p.Ala241Glyfs*106). This variant has previously been reported to be causative for congenital central hypoventilation syndrome (CCHS) and tumors of the sympathetic nervous system (Amiel et al. 2003. PubMed ID: 12640453; Trochet et al. 2005. PubMed ID: 16249188; Trochet et al. 2009. PubMed ID: 19058226; Di Lascio et al. 2018. PubMed ID: 29098737). This variant has not been reported in a large population database (http://gnomad.broadinstitute.org), and is interpreted as Pathogenic in ClinVar (https://www.ncbi.nlm.nih.gov/clinvar/variation/6010/). Frameshift variants in PHOX2B are expected to be pathogenic. This variant is interpreted as pathogenic. |
OMIM | RCV000006381 | SCV000026563 | pathogenic | Congenital central hypoventilation | 2003-04-01 | no assertion criteria provided | literature only |