Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Athena Diagnostics | RCV000201134 | SCV000255741 | pathogenic | Duchenne muscular dystrophy | 2012-06-30 | criteria provided, single submitter | clinical testing | |
Eurofins Ntd Llc |
RCV000733885 | SCV000861988 | pathogenic | not provided | 2018-06-21 | criteria provided, single submitter | clinical testing | |
ARUP Laboratories, |
RCV000733885 | SCV000885305 | pathogenic | not provided | 2018-06-20 | criteria provided, single submitter | clinical testing | The DMD c.5917C>T; p.Gln1973Ter variant (rs863225005) has been described in individuals affected with Duchenne muscular dystrophy (DMD) (Buzin 2005, Flanigan 2009). It is listed in ClinVar (Variation ID: 217206) and is absent from general population databases (1000 Genomes Project, Exome Variant Server, and Genome Aggregation Database), indicating it is not a common polymorphism. This variant induces an early termination codon and is predicted to result in a truncated protein or mRNA subject to nonsense-mediated decay. Additionally, several downstream nonsense variants have been reported in individuals with DMD and are considered pathogenic (see link to UMD-DMD database and references therein). Based on available information, this variant is considered pathogenic. Pathogenic variants in DMD are inherited in an X-linked manner and are associated with Duchenne muscular dystrophy (MIM: 310200), Becker muscular dystrophy (MIM: 300376), and dilated cardiomyopathy (MIM: 302045). References: Link to UMD-DMD database: http://www.umd.be/DMD/4DACTION/W_DMDT1/10 Buzin C et al. Mutation rates in the dystrophin gene: a hotspot of mutation at a CpG dinucleotide. Hum Mutat. 2005 Feb;25(2):177-88. Flanigan K et al. Mutational spectrum of DMD mutations in dystrophinopathy patients: application of modern diagnostic techniques to a large cohort. Hum Mutat. 2009 Dec;30(12):1657-66. |
Gene |
RCV000733885 | SCV000890258 | pathogenic | not provided | 2018-08-06 | criteria provided, single submitter | clinical testing | The Q1973X variant has been reported previously in association with dystrophinopathy, most often with Duchenne muscular dystrophy (Buzin et al., 2005; Flanigan et al., 2009). This variant is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The Q1973X variant is not observed in large population cohorts (Lek et al., 2016). |