Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002536209 | SCV003443049 | pathogenic | Rubinstein-Taybi syndrome | 2023-08-10 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. ClinVar contains an entry for this variant (Variation ID: 694820). Disruption of this splice site has been observed in individual(s) with Rubinstein-Taybi syndrome (PMID: 29132461). In at least one individual the variant was observed to be de novo. This variant is not present in population databases (gnomAD no frequency). This sequence change affects a donor splice site in intron 20 of the CREBBP gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in CREBBP are known to be pathogenic (PMID: 17052327, 18792986). |
Prevention |
RCV003413671 | SCV004114238 | pathogenic | CREBBP-related disorder | 2022-10-11 | criteria provided, single submitter | clinical testing | The CREBBP c.3779+1G>T variant is predicted to disrupt the GT donor site and interfere with normal splicing. This variant has been previously reported in individuals with Rubinstein-Taybi syndrome (Li et al. 2017. PubMed ID: 29132461; Cross et al. 2020. PubMed ID: 32827181), and in an individual with developmental disorder (reported with genomic position 3801726 in Table S2, Turner et al. 2019. PubMed ID: 31785789). An alternate nucleotide change (c.3779+1G>A) has also been reported in a large cohort of individuals with Rubinstein-Taibi syndrome (Cross et al. 2020. PubMed ID: 32827181). The c.3779+1G>T variant has not been reported in a large population database (http://gnomad.broadinstitute.org), indicating this variant is rare. Variants that disrupt the consensus splice donor site in CREBBP are expected to be pathogenic. This variant is interpreted as pathogenic. |
Gene |
RCV004721656 | SCV005327078 | pathogenic | not provided | 2023-08-18 | criteria provided, single submitter | clinical testing | Canonical splice site variant predicted to result in an in-frame loss of the adjacent exon in a gene for which loss of function is a known mechanism of disease; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 29132461, 32827181, 31785789) |
Wessex Regional Genetics Laboratory, |
RCV000856913 | SCV000999447 | pathogenic | Rubinstein-Taybi syndrome due to CREBBP mutations | 2019-11-05 | no assertion criteria provided | clinical testing |