Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000004708 | SCV000485611 | pathogenic | Nephropathic cystinosis | 2016-09-09 | criteria provided, single submitter | clinical testing | |
Invitae | RCV001044380 | SCV001208174 | pathogenic | Ocular cystinosis; Juvenile nephropathic cystinosis; Nephropathic cystinosis | 2019-12-12 | criteria provided, single submitter | clinical testing | This sequence change replaces glycine with arginine at codon 339 of the CTNS protein (p.Gly339Arg). The glycine residue is highly conserved and there is a moderate physicochemical difference between glycine and arginine. This variant is present in population databases (rs121908127, ExAC 0.01%). This variant has been reported to segregate with cystinosis in two families (PMID: 11565547) and it has been reported as homozygous or in combination with another CTNS variant in individuals affected with cystinosis (PMID: 23640116, 12825071, 21786142, 12204010, 11565547). ClinVar contains an entry for this variant (Variation ID: 4455). Experimental studies have shown that this missense change does not alter subcellular localization but abrogates CTNS transporter activity (PMID: 15128704). For these reasons, this variant has been classified as Pathogenic. |
Integrated Genetics/Laboratory Corporation of America | RCV001193377 | SCV001362153 | pathogenic | Cystinosis | 2019-09-16 | criteria provided, single submitter | clinical testing | Variant summary: CTNS c.1015G>A (p.Gly339Arg) results in a non-conservative amino acid change in the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 3.2e-05 in 251256 control chromosomes (gnomAD). c.1015G>A has been reported in the literature in multiple compound heterozygote and homozygote individuals affected with Cystinosis (eg- Mason_2003, Rupar_2001). These data indicate that the variant is very likely to be associated with disease. A ClinVar submission (evaluation after 2014) cites the variant as pathogenic. Based on the evidence outlined above, the variant was classified as pathogenic. |
OMIM | RCV000004708 | SCV000024883 | pathogenic | Nephropathic cystinosis | 2001-09-01 | no assertion criteria provided | literature only | |
Natera, |
RCV001193377 | SCV001463155 | pathogenic | Cystinosis | 2020-09-16 | no assertion criteria provided | clinical testing |