Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003064379 | SCV003443697 | uncertain significance | Ocular cystinosis; Juvenile nephropathic cystinosis; Inborn genetic diseases | 2022-07-16 | criteria provided, single submitter | clinical testing | This variant, c.1036_1047del, results in the deletion of 4 amino acid(s) of the CTNS protein (p.Asp346_Phe349del), but otherwise preserves the integrity of the reading frame. This variant is present in population databases (no rsID available, gnomAD 0.006%). This variant has been observed in individual(s) with cystinosis (PMID: 12442267). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. This variant is also known as c.1375-1386del12(DVVF346-349del). Algorithms developed to predict the effect of variants on protein structure and function are not available or were not evaluated for this variant. Experimental studies have shown that this variant affects CTNS function (PMID: 15128704). In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
Baylor Genetics | RCV003475497 | SCV004212976 | likely pathogenic | Nephropathic cystinosis | 2024-03-14 | criteria provided, single submitter | clinical testing |