Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genome- |
RCV001580688 | SCV001810388 | uncertain significance | Nephropathic cystinosis | 2021-07-22 | criteria provided, single submitter | clinical testing | |
Genome- |
RCV001580689 | SCV001810389 | uncertain significance | Juvenile nephropathic cystinosis | 2021-07-22 | criteria provided, single submitter | clinical testing | |
Genome- |
RCV001580690 | SCV001810390 | uncertain significance | Ocular cystinosis | 2021-07-22 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV002573265 | SCV003470620 | uncertain significance | Ocular cystinosis; Juvenile nephropathic cystinosis; Inborn genetic diseases | 2022-07-21 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 63 of the CTNS protein (p.Arg63Cys). This variant is present in population databases (rs555311279, gnomAD 0.009%). This variant has not been reported in the literature in individuals affected with CTNS-related conditions. ClinVar contains an entry for this variant (Variation ID: 1210394). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is not expected to disrupt CTNS protein function. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |