Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003765489 | SCV004571004 | pathogenic | Ocular cystinosis; Juvenile nephropathic cystinosis; Inborn genetic diseases | 2023-09-09 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (gnomAD no frequency). For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 253206). This premature translational stop signal has been observed in individual(s) with cystinosis (PMID: 28238446, 35513889). This sequence change creates a premature translational stop signal (p.Ser86Phefs*38) in the CTNS gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CTNS are known to be pathogenic (PMID: 9537412, 27102039). |
IUMS Hospital Medical Genetics Lab, |
RCV000239629 | SCV000297853 | pathogenic | Cystinosis | no assertion criteria provided | clinical testing | ||
Rasad Genetic Department, |
RCV002279718 | SCV002099449 | pathogenic | Nephropathic cystinosis | 2020-01-01 | no assertion criteria provided | clinical testing |