Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000588528 | SCV000698527 | pathogenic | Cystinosis | 2017-02-02 | criteria provided, single submitter | clinical testing | Variant summary: The CTNS c.853-2A>G variant involves the alteration of a conserved intronic nucleotide. One in silico tool predicts a damaging outcome for this variant. 4/4 splice prediction tools predict the complete loss of a canonical 5' splice acceptor site. These predictions have been confired by functional studies showing patient RNA having a transcript that contains the first 41bp of IVS10 and a deletion of the first 26 bp of exon11. This variant is absent in 118932 control chromosomes but has been reported in a severely affected proband in the literature. Taken together, this variant is classified as pathogenic. |
Counsyl | RCV000666666 | SCV000790995 | likely pathogenic | Nephropathic cystinosis | 2017-04-18 | criteria provided, single submitter | clinical testing | |
Baylor Genetics | RCV000666666 | SCV004212951 | pathogenic | Nephropathic cystinosis | 2023-09-17 | criteria provided, single submitter | clinical testing | |
Fulgent Genetics, |
RCV005091543 | SCV005641937 | likely pathogenic | Ocular cystinosis; Juvenile nephropathic cystinosis; Nephropathic cystinosis | 2024-04-06 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV005223021 | SCV005863179 | pathogenic | Ocular cystinosis; Juvenile nephropathic cystinosis; Inborn genetic diseases | 2024-08-31 | criteria provided, single submitter | clinical testing | This sequence change affects an acceptor splice site in intron 10 of the CTNS gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in CTNS are known to be pathogenic (PMID: 9537412, 27102039). This variant is present in population databases (no rsID available, gnomAD 0.0009%). Disruption of this splice site has been observed in individual(s) with cystinosis (PMID: 12442267, 29421779). This variant is also known as c.1192-2A>G. ClinVar contains an entry for this variant (Variation ID: 496277). Studies have shown that disruption of this splice site is associated with inconclusive levels of altered splicing (PMID: 12442267). For these reasons, this variant has been classified as Pathogenic. |