Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Congenital and Hereditary Diseases, |
RCV001375476 | SCV001554457 | likely pathogenic | Nephropathic cystinosis | 2021-03-01 | no assertion criteria provided | clinical testing | DNA sequencing revealed novel homozygous splicing mutation NM_001031681: c.971-1G>C in 6 patients belonging to 4 families. All parents of these patients were consanguineous and were confirmed to be heterozygous carriers. The splicing NM_001031681: c.971-1G>C segregated according to a recessive model with full penetrance. NM_001031681: c.971-1G>C was not referenced in the NHLBI Exome Variant Server or in the ClinVar database. Analysis of NM_001031681: c.971-1G>C with Alamut, predicted change at acceptor site of intron 11, 1 bp downstream and the activation of a cryptic acceptor site at +5 bp. The predicted protein will be p.D324VfsX31. |