Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Mendelics | RCV002247400 | SCV002518469 | uncertain significance | not specified | 2022-05-04 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV002247400 | SCV003922948 | uncertain significance | not specified | 2023-03-06 | criteria provided, single submitter | clinical testing | Variant summary: PFN1 c.350A>G (p.Glu117Gly) results in a non-conservative amino acid change in the encoded protein sequence. Three of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 0.0005 in 251482 control chromosomes. This frequency does not allow conclusions about variant significance. c.350A>G has been reported in the literature in individuals affected with PFN1-Related Disorders such as familial and sporadic Amyotrophic Lateral Sclerosis (ALS), Frontotemporal Dementia (FTD) and in unaffected controls with a reported moderate risk of association and a 95% CI that slightly overlaps 1 (example, PMID: 24309268). These report(s) do not provide unequivocal conclusions about an inherited penetrant association of the variant with PFN1-Related Disorders. Experimental evidence demonstrating an impact on protein function have suggested conflicting mechanism of action, namely gain of function due to TDP43 accumulation and loss of function due to altered stress granule dynamics (example, PMID: 26908597). One clinical diagnostic laboratory has submitted clinical-significance assessments for this variant to ClinVar after 2014 without evidence for independent evaluation and classified the variant as uncertain significance. Based on the evidence outlined above, the variant was classified as uncertain significance. |
Ce |
RCV005243103 | SCV005892732 | benign | not provided | 2025-02-01 | criteria provided, single submitter | clinical testing | PFN1: BS1, BS2 |
OMIM | RCV000030697 | SCV000053358 | pathogenic | Amyotrophic lateral sclerosis type 18 | 2012-08-23 | no assertion criteria provided | literature only |