Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Revvity Omics, |
RCV003132529 | SCV003813731 | uncertain significance | not provided | 2019-12-26 | criteria provided, single submitter | clinical testing | |
Baylor Genetics | RCV003463061 | SCV004206087 | likely pathogenic | Fetal akinesia deformation sequence 2 | 2024-02-19 | criteria provided, single submitter | clinical testing | |
Gene |
RCV003132529 | SCV005324897 | likely pathogenic | not provided | 2023-11-08 | criteria provided, single submitter | clinical testing | Observed as a homozygous variant in multiple affected and unaffected relatives in a family with limb-girdle type congenital myasthenic syndrome. Affected patients also carried a homozygous variant in another gene, suggesting digenic inheritance with the R164H variant possibly being a hypomorphic allele (PMID: 27966543); Published functional studies suggest that this variant weakens the self-association of the protein and impairs end-plate acetylcholine receptor clustering (PMID: 34033754); Not observed at significant frequency in large population cohorts (gnomAD); Located within TPR5 domain (PMID: 22678886); In silico analysis supports that this missense variant does not alter protein structure/function; This variant is associated with the following publications: (PMID: 34426522, 34139178, 22678886, 27966543, 19620612, 34033754) |