Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000301725 | SCV000341224 | uncertain significance | not provided | 2016-04-15 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000697680 | SCV000826305 | likely pathogenic | GNE myopathy; Sialuria | 2024-01-02 | criteria provided, single submitter | clinical testing | This sequence change falls in intron 6 of the GNE gene. It does not directly change the encoded amino acid sequence of the GNE protein. It affects a nucleotide within the consensus splice site. This variant is not present in population databases (gnomAD no frequency). This variant has been observed in individual(s) with hereditary inclusion-body myopathy (PMID: 15146476, 22231866). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. This variant is also known as c.1070+2dupT. ClinVar contains an entry for this variant (Variation ID: 287448). Variants that disrupt the consensus splice site are a relatively common cause of aberrant splicing (PMID: 17576681, 9536098). Studies have shown that this variant is associated with inconclusive levels of altered splicing (PMID: 15146476). In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |