Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000665671 | SCV000789830 | likely pathogenic | GNE myopathy | 2017-02-22 | criteria provided, single submitter | clinical testing | |
Revvity Omics, |
RCV001784233 | SCV002018492 | likely pathogenic | not provided | 2019-11-13 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV002530662 | SCV003441378 | pathogenic | GNE myopathy; Sialuria | 2022-11-01 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This sequence change replaces arginine, which is basic and polar, with tryptophan, which is neutral and slightly polar, at codon 42 of the GNE protein (p.Arg42Trp). This variant is present in population databases (rs769716748, gnomAD 0.003%). This missense change has been observed in individuals with distal myopathy (PMID: 14972325, 29480215, 33250842). This variant is also known as R11W. ClinVar contains an entry for this variant (Variation ID: 550820). Algorithms developed to predict the effect of missense changes on protein structure and function (SIFT, PolyPhen-2, Align-GVGD) all suggest that this variant is likely to be disruptive. Experimental studies have shown that this missense change affects GNE function (PMID: 16503651). This variant disrupts the p.Arg42 amino acid residue in GNE. Other variant(s) that disrupt this residue have been determined to be pathogenic (Invitae). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. |
Laboratorio de Genetica e Diagnostico Molecular, |
RCV000665671 | SCV003807685 | likely pathogenic | GNE myopathy | 2022-09-16 | criteria provided, single submitter | clinical testing | ACMG classification criteria: PS3 supporting, PS4 moderated, PM2 moderated, PM3 moderated, PM5 moderated, PP3 supporting |
Baylor Genetics | RCV000665671 | SCV004191648 | likely pathogenic | GNE myopathy | 2024-03-12 | criteria provided, single submitter | clinical testing |