Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Medicine for Neurodegenerative and Neuromuscular Diseases Unit, |
RCV001647167 | SCV001519155 | pathogenic | Ataxia - intellectual disability - oculomotor apraxia - cerebellar cysts syndrome | 2021-01-04 | criteria provided, single submitter | research | |
DASA | RCV001647167 | SCV002499415 | likely pathogenic | Ataxia - intellectual disability - oculomotor apraxia - cerebellar cysts syndrome | 2022-04-10 | criteria provided, single submitter | clinical testing | The c.184C>T;p.(Arg62*) variant creates a premature translational stop signal in the LAMA1 gene. It is expected to result in an absent or disrupted protein product -PVS1. The variant is present at low allele frequencies population databases (rs758223206 – gnomAD 0.00007964%; ABraOM 0.000427 frequency - https://abraom.ib.usp.br/) - PM2_supporting. In summary, the currently available evidence indicates that the variant is likely pathogenic. |