Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Provincial Medical Genetics Program of British Columbia, |
RCV002211033 | SCV002496391 | pathogenic | Ataxia - intellectual disability - oculomotor apraxia - cerebellar cysts syndrome | 2022-01-01 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003101224 | SCV003442573 | pathogenic | not provided | 2023-08-04 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 1675304). This premature translational stop signal has been observed in individual(s) with Poretti-Boltshauser syndrome (PMID: 26932191). This variant is present in population databases (rs767943611, gnomAD 0.005%). This sequence change creates a premature translational stop signal (p.Arg1307*) in the LAMA1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in LAMA1 are known to be pathogenic (PMID: 25105227, 26932191). |