Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002465388 | SCV004809058 | pathogenic | Creatine transporter deficiency | 2024-02-22 | reviewed by expert panel | curation | The NM_005629.4: c.1428C>G (p.Tyr476Ter) variant in SLC6A8 is a nonsense variant predicted to cause a premature stop codon in biologically-relevant-exon 10/13, leading to nonsense mediated decay in a gene in which loss-of-function is an established disease mechanism (PVS1). This variant has been reported a male with intellectual disability, autistic features, seizures and absent creatine peak on brain MRS (PMID: 29435807) (PP4). The variant is absent in gnomAD v2.1.1. (PM2_Supporting). There is a ClinVar entry for this variant (Variation ID: 1802549). In summary, this variant meets the criteria to be classified as pathogenic for creatine transporter deficiency. SLC6A8-specific criteria applied, as specified by the ClinGen CCDS VCEP (Specifications Version 1.1.0): PVS1, PP4, PM2_Supporting. (Classification approved by the ClinGen Cerebral Creatine Deficiency Syndromes Variant Curation Expert Panel on February 22, 2024). |
Laboratory of Medical Genetics, |
RCV002465388 | SCV002760055 | likely pathogenic | Creatine transporter deficiency | 2022-11-29 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV002465388 | SCV005840553 | pathogenic | Creatine transporter deficiency | 2025-01-19 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Tyr476*) in the SLC6A8 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in SLC6A8 are known to be pathogenic (PMID: 22281021). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with creatine transporter deficiency (PMID: 29435807). ClinVar contains an entry for this variant (Variation ID: 1802549). For these reasons, this variant has been classified as Pathogenic. |