Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV004491273 | SCV004990790 | likely pathogenic | Inborn genetic diseases | 2023-09-20 | criteria provided, single submitter | clinical testing | The c.404G>A (p.R135H) alteration is located in exon 1 (coding exon 1) of the NR2F1 gene. This alteration results from a G to A substitution at nucleotide position 404, causing the arginine (R) at amino acid position 135 to be replaced by a histidine (H). This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). Two other alterations at the same codon, c.403C>T (p.R135C) and c.403C>A (p.R135S), have been detected in patients with symptoms consistent with Bosch-Boonstra-Schaaf optic atrophy syndrome. This amino acid position is highly conserved in available vertebrate species. Based on internal structural analysis, R135H is moderately disruptive to the DNA-binding interface of NR2F1, but there are no comparable internally pathogenic variants nearby for comparison (Liu, 2023). This alteration is predicted to be deleterious by in silico analysis. Based on the available evidence, this alteration is classified as likely pathogenic. |