Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Broad Center for Mendelian Genomics, |
RCV002227844 | SCV002507002 | uncertain significance | Congenital myasthenic syndrome 5 | 2022-05-04 | criteria provided, single submitter | curation | The homozygous p.Cys440Tyr variant in COLQ was identified by our study in 1 individual with congenital myasthenic syndrome 5. The variant has not been previously reported in individuals with congenital myasthenic syndrome 5 and was absent from large population studies. Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. In summary, while there is some suspicion for a pathogenic role, the clinical significance of this variant is uncertain. ACMG/AMP Criteria applied: PM2, PM3_supporting, PP3 (Richards 2015). |