Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Hudson |
RCV000035018 | SCV000992582 | likely pathogenic | 2-hydroxyglutaric aciduria | 2019-07-23 | criteria provided, single submitter | research | ACMG codes: PS3, PM2, PM3, PP3 |
Institute of Human Genetics, |
RCV000035018 | SCV001934316 | pathogenic | 2-hydroxyglutaric aciduria | 2020-11-12 | criteria provided, single submitter | clinical testing | This variant was identified as compound heterozygous with NM_005984.5:c.578C>T. |
Labcorp Genetics |
RCV001852702 | SCV002290314 | likely pathogenic | not provided | 2021-10-11 | criteria provided, single submitter | clinical testing | This variant is present in population databases (rs431905509, ExAC 0.005%). This missense change has been observed in individuals with combined D-2- and L-2-hydroxyglutaric aciduria (PMID: 23561848, 29238895). ClinVar contains an entry for this variant (Variation ID: 42194). Algorithms developed to predict the effect of missense changes on protein structure and function (SIFT, PolyPhen-2, Align-GVGD) all suggest that this variant is likely to be disruptive. Experimental studies have shown that this missense change affects SLC25A1 function (PMID: 9031613, 29238895). This variant disrupts the p.Arg282 amino acid residue in SLC25A1. Other variant(s) that disrupt this residue have been observed in individuals with SLC25A1-related conditions (PMID: 23393310, 23561848, 29238895), which suggests that this may be a clinically significant amino acid residue. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. This sequence change replaces arginine with cysteine at codon 282 of the SLC25A1 protein (p.Arg282Cys). The arginine residue is highly conserved and there is a large physicochemical difference between arginine and cysteine. |
Gene |
RCV001852702 | SCV004036393 | pathogenic | not provided | 2023-03-21 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect on enzyme activity (Pop et al., 2018; Majd et al., 2018); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 29238895, 23561848, 34930662, 29031613) |
Neuberg Centre For Genomic Medicine, |
RCV001801242 | SCV004175826 | pathogenic | D,L-2-hydroxyglutaric aciduria | 2023-02-14 | criteria provided, single submitter | clinical testing | |
OMIM | RCV001801242 | SCV000058658 | pathogenic | D,L-2-hydroxyglutaric aciduria | 2013-04-04 | no assertion criteria provided | literature only |