Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV000152660 | SCV000202014 | pathogenic | Rare genetic deafness | 2013-06-05 | criteria provided, single submitter | clinical testing | The Val483fs variant in WFS1 has been reported in the homozygous state in one Sa udi Arabian individual with clinical features of Wolfram syndrome, also known as DIDMOAD (Inoue 1998). This frameshift variant is predicted to alter the protei n?s amino acid sequence beginning at position 483 and lead to a premature termin ation codon 62 amino acids downstream. This alteration is then predicted to lead to a truncated or absent protein. Truncating variants in WFS1 are established a s pathogenic for Wolfram syndrome. In summary, this variant meets our criteria t o be classified as pathogenic (http://www.pcpgm.partners.org/lmm). |
Clinical Genomics, |
RCV002273965 | SCV003801368 | likely pathogenic | Wolfram syndrome 1 | criteria provided, single submitter | research | Potent mutations in WFS1 gene are associated with Wolfram's syndrome, an autosomal recessive condition, which cause diabetes mellitus, diabetes insipidus, deafness and optic atrophy. However no sufficient evidence is found to ascertain the role of this particular variant rs727503745 in Wolfram's syndrome yet. | |
OMIM | RCV002273965 | SCV000024947 | pathogenic | Wolfram syndrome 1 | 1998-10-01 | no assertion criteria provided | literature only |