Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000004917 | SCV001202665 | pathogenic | Kostmann syndrome | 2022-12-23 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 4654). This premature translational stop signal has been observed in individual(s) with severe congenital neutropenia (PMID: 17187068, 18055975, 18330843, 18611981, 28102861). This variant is present in population databases (rs121908165, gnomAD 0.02%). This sequence change creates a premature translational stop signal (p.Arg86*) in the HAX1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in HAX1 are known to be pathogenic (PMID: 17187068). |
OMIM | RCV000004917 | SCV000025093 | pathogenic | Kostmann syndrome | 2008-12-01 | no assertion criteria provided | literature only | |
Natera, |
RCV000004917 | SCV001461737 | pathogenic | Kostmann syndrome | 2020-09-16 | no assertion criteria provided | clinical testing | |
Joint Genome Diagnostic Labs from Nijmegen and Maastricht, |
RCV001723537 | SCV001958289 | pathogenic | not provided | no assertion criteria provided | clinical testing | ||
Clinical Genetics DNA and cytogenetics Diagnostics Lab, |
RCV001723537 | SCV001968710 | pathogenic | not provided | no assertion criteria provided | clinical testing |