Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Endocrinology Unit / Unidade de Endocrinologia Genetica - |
RCV003228694 | SCV003924073 | pathogenic | Acromesomelic dysplasia 4 | 2023-05-11 | criteria provided, single submitter | clinical testing | The c.1154+1G>A variant occurs in a splice consensus site, predicted to alter splicing and result in a loss or disruption of normal protein function (PVS1). The variant is absent in most population databases (genomAD) and has a low frequency in the Brazilian population (MAF 0.000427, https://abraom.ib.usp.br/) (PM2). The patient's phenotype is compatible with the diagnosis of Acromesomelic dysplasia, without other genetic alterations that explain the phenotype (PP4). This variant was identified in homozygous in affected patient. |