Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000009007 | SCV001201650 | pathogenic | Niemann-Pick disease, type C2 | 2023-04-12 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Experimental studies have shown that this missense change affects NPC2 function (PMID: 18772377). An algorithm developed to predict the effect of missense changes on protein structure and function (PolyPhen-2) suggests that this variant is likely to be disruptive. ClinVar contains an entry for this variant (Variation ID: 8486). This missense change has been observed in individual(s) with Niemann-Pick disease type C (PMID: 16126423, 23791309). It has also been observed to segregate with disease in related individuals. This variant is present in population databases (rs104894458, gnomAD 0.003%). This sequence change replaces proline, which is neutral and non-polar, with serine, which is neutral and polar, at codon 120 of the NPC2 protein (p.Pro120Ser). |
OMIM | RCV000009007 | SCV000029221 | pathogenic | Niemann-Pick disease, type C2 | 2007-04-01 | no assertion criteria provided | literature only | |
Clinical Genetics Laboratory, |
RCV001528117 | SCV001739322 | pathogenic | Niemann-Pick disease, type C1 | 2021-02-09 | no assertion criteria provided | clinical testing |