Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Department Of Genetics, |
RCV000761519 | SCV000891650 | pathogenic | PYCR1-related de Barsy syndrome | 2017-12-30 | criteria provided, single submitter | curation | |
Baylor Genetics | RCV000014084 | SCV001525292 | pathogenic | Autosomal recessive cutis laxa type 2B | 2020-01-20 | criteria provided, single submitter | clinical testing | This variant was determined to be pathogenic according to ACMG Guidelines, 2015 [PMID:25741868]. |
Institute of Medical Genetics and Applied Genomics, |
RCV001543486 | SCV001762086 | likely pathogenic | not provided | 2021-06-17 | criteria provided, single submitter | clinical testing | |
Gene |
RCV001543486 | SCV003930944 | pathogenic | not provided | 2023-06-05 | criteria provided, single submitter | clinical testing | Functional studies using recombinant protein expressed and purified in E.coli showed negligible enzyme activity (Li et al., 2017); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 18348262, 19648921, 30450527, 28194412) |
Labcorp Genetics |
RCV001543486 | SCV005837783 | likely pathogenic | not provided | 2024-08-04 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with histidine, which is basic and polar, at codon 119 of the PYCR1 protein (p.Arg119His). This variant is present in population databases (rs121918377, gnomAD 0.007%). This missense change has been observed in individuals with autosomal recessive cutis laxa (PMID: 19648921, 23963297, 30450527). ClinVar contains an entry for this variant (Variation ID: 13197). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt PYCR1 protein function with a positive predictive value of 80%. Experimental studies have shown that this missense change affects PYCR1 function (PMID: 28194412). This variant disrupts the p.Arg119 amino acid residue in PYCR1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 23963297, 24035636, 25865492, 30450527). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
OMIM | RCV000014084 | SCV000034332 | pathogenic | Autosomal recessive cutis laxa type 2B | 2009-09-01 | no assertion criteria provided | literature only | |
University of Washington Center for Mendelian Genomics, |
RCV001291133 | SCV001479509 | likely pathogenic | Wiedemann-Rautenstrauch-like progeroid syndrome | no assertion criteria provided | research |