Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clinical Genetics Laboratory, |
RCV003325934 | SCV004031459 | likely pathogenic | Trichothiodystrophy 5, nonphotosensitive | 2023-09-01 | criteria provided, single submitter | clinical testing | The Tyr297Cysfs*3 variant was observed in a child with short stature, dry-skin, sparse hair and global developmental delay. It is a Null variant (frame-shift), predicted to cause NMD. Loss-of-function is a known mechanism of disease (gene has 3 reported pathogenic LOF variants). It is also absent from controls. In summary, the Tyr297Cysfs*3 variant meets ACMG criteria to be classified as pathogenic. |