Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Medicine for Neurodegenerative and Neuromuscular Diseases Unit, |
RCV001647198 | SCV001519179 | pathogenic | Neonatal pseudo-hydrocephalic progeroid syndrome | 2021-01-04 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV002546247 | SCV003330553 | pathogenic | not provided | 2022-03-13 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 1027476). This variant has not been reported in the literature in individuals affected with POLR3A-related conditions. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Met1280Ilefs*20) in the POLR3A gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in POLR3A are known to be pathogenic (PMID: 21855841, 25339210, 27612211, 30414627, 30450527). |