Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
The Division of Genetics and Genomic Medicine, |
RCV003333707 | SCV004041577 | likely pathogenic | Childhood Onset VCP-related Neurodevelopmental Disorder | 2023-09-01 | criteria provided, single submitter | clinical testing | This variant was detected using a 500-gene panel from the Molecular Genetics Laboratory at Brest University Hospital in a male child with developmental delay, epilepsy and macrocephaly. It is not present in gnomAD and is predicted to be deleterious by multiple algorithms (REVEL score 0.89). De novo inheritance was confirmed by Sanger sequencing of his parents. In vitro ATPase assays show this variant has increased ATPase activity compared to wildtype (Mah-Som et al, 2023). |
Molecular Genetics Lab, |
RCV003883215 | SCV004697744 | likely pathogenic | Inclusion body myopathy with Paget disease of bone and frontotemporal dementia type 1; Frontotemporal dementia and/or amyotrophic lateral sclerosis 6; Charcot-Marie-Tooth disease type 2Y | criteria provided, single submitter | clinical testing |