Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV004760768 | SCV005367986 | likely pathogenic | RASopathy | 2024-09-17 | reviewed by expert panel | curation | The c.208G>A (p.Ala70Thr) variant in RRAS2 is a missense variant predicted to cause substitution of alanine by threonine at amino acid 70. The highest population filtering allele frequency in gnomAD v2.1.1 is 0.00001084 (2/30538 alleles) in the South Asian population (PM2_Supporting, BS1, and BA1 are not met). The computational predictor REVEL gives a score of 0.863, which is above the threshold of 0.7, evidence that correlates with impact to RRAS2 function (PP3). This variant resides within the Switch II domain (amino acids 68 – 75), of RRAS2 that is defined as a critical functional domain by the ClinGen RASopathy VCEP (PM1). ERK Activation in HEK293T cells showed constitutive promotion of increased ERK phosphorylation indicating that this variant impacts protein function (PMID:31130282)(PS3_Supporting). This variant has been reported in 2 probands with features of RASopathy (PS4_Supporting; PMID:31130282). This variant has been identified as a de novo occurrence with confirmed parental relationships in 1 individual with features of RASopathy (PS2; PMID:31130282). In summary, this variant meets the criteria to be classified as likely pathogenic for autosomal dominant RASopathy based on the ACMG/AMP criteria applied, as specified by the ClinGen RASopathy VCEP: PS2, PM1, PS3_Supporting, PS4_Supporting, PP3. (RASopathy VCEP specifications version 1.1; 9/17/2024) |
Tartaglia Lab, |
RCV000852397 | SCV000902251 | pathogenic | Noonan syndrome | 2019-04-01 | criteria provided, single submitter | research | this is a pathogenic variant associated with Noonan Syndrome |
Prevention |
RCV003411705 | SCV004115267 | uncertain significance | RRAS2-related disorder | 2023-02-20 | criteria provided, single submitter | clinical testing | The RRAS2 c.208G>A variant is predicted to result in the amino acid substitution p.Ala70Thr. This variant was reported to segregate with disease in a three generation family with Noonan syndrome (Capri et al. 2019. PubMed ID: 31130282). Functional studies demonstrate this variant results in increased p-MEK/ERK levels, consistent with a gain-of-function mechanism, resulting in hyperactivation of the RAS pathway (Capri et al. 2019. PubMed ID: 31130282). This variant is reported in 0.0065% of alleles in individuals of South Asian descent in gnomAD (http://gnomad.broadinstitute.org/variant/11-14316397-C-T). Although we suspect that this variant may be pathogenic, at this time, the clinical significance of this variant is uncertain due to the absence of conclusive functional and genetic evidence. |
Institute of Human Genetics, |
RCV000853183 | SCV005397117 | likely pathogenic | Noonan syndrome 12 | 2024-10-30 | criteria provided, single submitter | clinical testing | Criteria applied: PS2,PM1,PS3_SUP,PS4_SUP,PP3 |
OMIM | RCV000853183 | SCV000995987 | pathogenic | Noonan syndrome 12 | 2019-10-15 | no assertion criteria provided | literature only |