Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002000195 | SCV002228958 | pathogenic | Frontotemporal dementia and/or amyotrophic lateral sclerosis 4 | 2024-08-31 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with glutamine, which is neutral and polar, at codon 357 of the TBK1 protein (p.Arg357Gln). This variant is present in population databases (rs758357594, gnomAD 0.004%). This missense change has been observed in individuals with amyotrophic lateral sclerosis (PMID: 25803835, 28822984, 30033073, 31000212). ClinVar contains an entry for this variant (Variation ID: 1453239). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) indicates that this missense variant is not expected to disrupt TBK1 protein function with a negative predictive value of 95%. Experimental studies have shown that this missense change affects TBK1 function (PMID: 25803835, 28822984). For these reasons, this variant has been classified as Pathogenic. |