Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Genetics Department, |
RCV003985998 | SCV004801823 | likely pathogenic | KBG syndrome | criteria provided, single submitter | clinical testing | A previously undescribed nucleotide variant creates a premature translation stop signal p.Lys2423Ter in the ANKRD11 gene. The variant was observed in heterozygous state in an individual affected with neck hygroma, hypertrophic cardiomyopathy, and dysmorphic features. Loss-of-function variants are reported in patients with KBG syndrome (OMIM: 148050). The variant is not present in population database (gnomAD no frequency). In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as likely pathogenic. |