Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000169220 | SCV000220485 | likely pathogenic | Charlevoix-Saguenay spastic ataxia | 2014-07-07 | criteria provided, single submitter | literature only | |
Labcorp Genetics |
RCV001850393 | SCV002174456 | pathogenic | Spastic paraplegia | 2024-01-25 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg4078*) in the SACS gene. While this is not anticipated to result in nonsense mediated decay, it is expected to disrupt the last 502 amino acid(s) of the SACS protein. This variant is present in population databases (rs141315518, gnomAD 0.003%). This premature translational stop signal has been observed in individual(s) with spastic ataxia of Charlevoix-Saguenay (PMID: 22816526). ClinVar contains an entry for this variant (Variation ID: 188867). This variant disrupts a region of the SACS protein in which other variant(s) (p.Tyr4538* ) have been determined to be pathogenic (Invitae). This suggests that this is a clinically significant region of the protein, and that variants that disrupt it are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV002509271 | SCV002819085 | likely pathogenic | not provided | 2022-07-06 | criteria provided, single submitter | clinical testing | Reported in an individual with autosomal recessive spastic ataxia of Charlevoix-Saguenay (ARSACS), however segregation information was not provided (Prodi et al., 2013); Nonsense variant predicted to result in protein truncation in a gene for which loss of function is a known mechanism of disease; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 22816526, 31589614) |
Baylor Genetics | RCV000169220 | SCV004202281 | pathogenic | Charlevoix-Saguenay spastic ataxia | 2024-03-24 | criteria provided, single submitter | clinical testing |