Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Department of Genetics, |
RCV001733859 | SCV001983779 | pathogenic | Radio-Tartaglia syndrome | 2021-10-27 | no assertion criteria provided | clinical testing | This variant is absent from the gnomAD database. The probability of loss-of-function intolerance (pLI) of this gene is 1 in the gnomAD browser, which suggests that SPEN is highly intolerant to heterozygous loss-of-function variants. SPEN is also reported to be enriched in de novo and truncating variants in patients with a developmental disorder (Wang et al. 2020; Radio et al. 2021). It encodes a transcriptional repressor with a major role in the initiation of X chromosome inactivation (Dossin et al. 2020). Pathogenic variations in SPEN have been very recently associated with a neurodevelopmental disease in two clinical cohorts (Wang et al. 2020; Radio et al. 2021). The patient's phenotype appears to be consistent with the descriptions in the literature. |