Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Shenzhen Institute of Pediatrics, |
RCV000495259 | SCV000583549 | pathogenic | Short stature-optic atrophy-Pelger-HuC+t anomaly syndrome | 2017-07-11 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003558401 | SCV004292059 | pathogenic | not provided | 2023-03-29 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 430659). This premature translational stop signal has been observed in individual(s) with recurrent acute liver failure (PMID: 28629372). This variant is present in population databases (no rsID available, gnomAD 0.1%). This sequence change creates a premature translational stop signal (p.Gln196*) in the NBAS gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in NBAS are known to be pathogenic (PMID: 26073778, 26541327, 27789416, 28031453). |