Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV001818170 | SCV002067345 | pathogenic | not provided | 2019-07-18 | criteria provided, single submitter | clinical testing | DNA sequence analysis of the SBDS gene demonstrated a sequence change in the canonical splice donor site of intron 4, c.624+1G>C. This sequence change has been previously described in compound heterozygous state with the c.258+2T>C pathogenic sequence change in a patient with an atypical Schwachman-Bodian-Diamond syndrome phenotype, with low neutrophil count and mild to moderate thrombocytopenia but no apparent extrahaematological features of SBDS (PMID 21659346). The c.624+1G>C sequence change is absent from large population databases such as ExAC and gnomAD. This pathogenic sequence change is predicted to affect normal splicing of the SBDS gene and result in an abnormal protein. |
Gene |
RCV000020732 | SCV000041307 | not provided | Shwachman-Diamond syndrome 1 | no assertion provided | literature only |