Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000672305 | SCV000797402 | likely pathogenic | Bardet-Biedl syndrome 13; Meckel syndrome, type 1; Joubert syndrome 28 | 2018-01-30 | criteria provided, single submitter | clinical testing | |
Molecular Genetics, |
RCV002225110 | SCV002503722 | uncertain significance | Joubert syndrome 28 | 2023-03-30 | criteria provided, single submitter | clinical testing | This sequence change affects the canonical donor splice site in intron 18 of MKS1. It is expected to disrupt RNA splicing and likely results in cryptic donor site usage leading to intron inclusion of 21 bp (SpliceAI). The predicted effect is an in-frame insertion of 7 amino acids in a region with no known functional domain. This has not been confirmed using RNA studies. The variant is present in a single individual in a large population cohort (rs756102768, 1/249,584 alleles, 0 homozygotes in gnomAD v2.1), and has been reported as likely pathogenic previously (ClinVar). The variant has not been reported in the relevant medical literature. Based on the classification scheme RMH Modified ACMG Guidelines v1.3.0, this variant is classified as a VARIANT OF UNCERTAIN SIGNIFICANCE. Following criteria are met: PVS1_Moderate, PM2_Supporting. |
Labcorp Genetics |
RCV003767996 | SCV004588224 | likely pathogenic | Familial aplasia of the vermis; Meckel-Gruber syndrome | 2023-10-22 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 8 of the MKS1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in MKS1 are known to be pathogenic (PMID: 19466712, 24886560, 26490104). This variant is present in population databases (rs756102768, gnomAD 0.0009%). This variant has not been reported in the literature in individuals affected with MKS1-related conditions. ClinVar contains an entry for this variant (Variation ID: 556312). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |