Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Broad Center for Mendelian Genomics, |
RCV002790008 | SCV003761350 | uncertain significance | Hypomyelinating leukodystrophy 8 with or without oligodontia and-or hypogonadotropic hypogonadism | 2022-02-24 | criteria provided, single submitter | curation | The p.Arg329Gln variant in POLR3B has been reported in 1 individual in the compound heterozygous state with 4H leukodystrophy (PMID: 25131622) and has been identified in 0.0009% (1/113512) of European (non-Finnish) chromosomes by the Genome Aggregation Database (gnomAD, http://gnomad.broadinstitute.org; dbSNP ID:rs1337382297). Although this variant has been seen in the general population in a heterozygous state, its frequency is low enough to be consistent with a recessive carrier frequency. Computational prediction tools and conservation analyses do not provide strong support for or against an impact to the protein. The number of missense variants reported in POLR3B in the general population is lower than expected, suggesting there is little benign variation in this gene and slightly increasing the possibility that a missense variant in this gene may not be tolerated. In summary, the clinical significance of the p.Arg329Gln variant is uncertain. ACMG/AMP Criteria applied: PM2_supporting, PM3_supporting, PP2 (Richards 2015). |
Baylor Genetics | RCV002790008 | SCV004040669 | likely pathogenic | Hypomyelinating leukodystrophy 8 with or without oligodontia and-or hypogonadotropic hypogonadism | 2023-04-07 | criteria provided, single submitter | clinical testing | |
Prevention |
RCV004554025 | SCV004118706 | likely pathogenic | POLR3B-related disorder | 2024-07-12 | no assertion criteria provided | clinical testing | The POLR3B c.986G>A variant is predicted to result in the amino acid substitution p.Arg329Gln. This variant has been reported in the compound heterozygous state in patients with POLR3B related autosomal recessive disease (Srivastava et al. 2014. PubMed ID: 25131622; PreventionGenetics internal data). This variant is reported in 0.00088% of alleles in individuals of European (Non-Finnish) descent in gnomAD. This variant is interpreted as likely pathogenic. |