Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
3billion | RCV003152935 | SCV003841502 | likely pathogenic | Leukoencephalopathy with brain stem and spinal cord involvement-high lactate syndrome | 2023-02-23 | criteria provided, single submitter | clinical testing | The variant is observed at an extremely low frequency in the gnomAD v2.1.1 dataset (total allele frequency: <0.001%). Functional studies provide moderate evidence of the variant having a damaging effect on the gene or gene product (PMID: 33977142). In silico tool predictions suggest damaging effect of the variant on gene or gene product (REVEL: 0.87; 3Cnet: 0.97). Same nucleotide change resulting in same amino acid change has been previously reported to be associated with DARS2-related disorder (PMID: 33977142). Therefore, this variant is classified as Likely pathogenic according to the recommendation of ACMG/AMP guideline. |