Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
DASA | RCV001824200 | SCV002073781 | likely pathogenic | Charcot-Marie-Tooth disease axonal type 2Q | 2022-02-05 | criteria provided, single submitter | clinical testing | The c.1409del;p.(Gly470Aspfs*3) is a null frameshift variant (NMD) in the DHTKD1 gene and predicts alteration of the nonsense-mediate decay - NMD is present in a relevant exon to the transcript - PVS1. This variant is not present in population databases (rs1281526839, gnomAD; ABraOM no frequency - http://abraom.ib.usp.br/) - PM2. In summary, the currently available evidence indicates that the variant is likely pathogenic. |
Labcorp Genetics |
RCV001869830 | SCV002186129 | pathogenic | 2-aminoadipic 2-oxoadipic aciduria | 2021-11-26 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant has not been reported in the literature in individuals affected with DHTKD1-related conditions. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Gly470Aspfs*3) in the DHTKD1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in DHTKD1 are known to be pathogenic (PMID: 23141293, 25860818). |