Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Medicine for Neurodegenerative and Neuromuscular Diseases Unit, |
RCV001647192 | SCV001519113 | likely pathogenic | Spinocerebellar ataxia type 42 | 2021-01-04 | criteria provided, single submitter | research | |
Gene |
RCV004727150 | SCV005331894 | uncertain significance | not provided | 2023-05-17 | criteria provided, single submitter | clinical testing | Reported in an individual with late onset spinocerebellar ataxia (Galatolo et al., 2021); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant does not alter protein structure/function; This variant is associated with the following publications: (PMID: 34445196) |